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Gene editing restores dystrophin expression in a canine model of Duchenne muscular dystrophy 期刊论文
SCIENCE, 2018, 362 (6410) : 86-90
作者:  Amoasii, Leonela;  Hildyard, John C. W.;  Li, Hui;  Sanchez-Ortiz, Efrain;  Mireault, Alex;  Caballero, Daniel;  Harron, Rachel;  Stathopoulou, Thaleia-Rengina;  Massey, Claire;  Shelton, John M.;  Bassel-Duby, Rhonda;  Piercy, Richard J.;  Olson, Eric N.
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