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Gene correction for SCID-X1 in long-term hematopoietic stem cells (vol 10, 1634, 2019) 期刊论文
NATURE COMMUNICATIONS, 2019, 10
作者:  Pavel-Dinu, Mara;  Wiebking, Volker;  Dejene, Beruh T.;  Srifa, Waracharee;  Mantri, Sruthi;  Nicolas, Carmencita E.;  Lee, Ciaran;  Bao, Gang;  Kildebeck, Eric J.;  Punjya, Niraj;  Sindhu, Camille;  Inlay, Matthew A.;  Saxena, Nivedita;  DeRavin, Suk See;  Malech, Harry;  Roncarolo, Maria Grazia;  Weinberg, Kenneth I.;  Porteus, Matthew H.
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